U.S. doctors are getting the word out about how to spot a rare measles complication that had been a relic of the past: subacute sclerosing panencephalitis. It affects a person years after a measles ...

Cannabis is one of the most widely studied plants in the world today. Many people know it because of compounds such as THC ...

One mother told Newsweek she was "terrified" of losing access to the drug her daughter relies on as a result of an FDA rejection.

AstraZeneca, a global, science-led biopharmaceutical company, has made available its treatment, Soliris®, in Malaysia as part of its ongoing ...

Life-saving treatments for children with orphan illnesses often move slowly, if at all, through the federal approval process.

Tasha Faruqui, 44, is a working mom in Cincinnati, Ohio. Her daughter, 13-year-old Soraya, is dying of a rare disease.

Some less common but serious side effects of gabapentin include suicidal thoughts, allergic reactions, and serious breathing ...

TikToker Audrey (@audreykandil) is a stay-at-home mom to a medically complex child. She and her husband both have medical backgrounds, which makes caretaking easier and harder at the same time. Her ...

"CNBC Cures: Defying Rare Disease" will air on Thursday, March 19 at 7PM ET.

Haunted by the cystic fibrosis patients he could not help, one Iowa doctor commits his life to understanding what is broken deep inside their cells.

In a bar, a poet meets the man behind the drug that saved his life — discovering how science, faith and chance created a future thought impossible.

Maria Baum, a 22-year-old Ohio resident born with Williams syndrome, has defied medical odds while pursuing her passion for ...