Nemours Children's Hospital offers new gene therapy for sickle cell

Nemours Children's Hospital is now offering Lyfgenia gene therapy. The treatment aims to reduce pain crises and hospital visits for young patients.

Gene Simmons Says He Would've 'Gone Down the Rabbit Hole into Darkness' Without Wife Shannon Tweed

Simmons and Tweed tied the knot in 2011, after 28 years of dating ...

Gene Simmons Recalls Sticking His Tongue 'Almost Down' Adam Sandler's Throat Because He Wanted to 'Turn Adam into My Bitch'

Gene Simmons said he once stuck his tongue "almost down" Adam Sandler's throat at a party. Sandler previously gave his version of the story on 'Conan.' ...
Page Six

Inside Gene Hackman’s $80 million estate drama one year after actor’s shocking death

Gene Hackman’s reported $80 million estate is at the center of legal drama — one year after the legendary actor’s heartbreaking death. Hackman and his wife, Betsy Arakawa, were found dead in their ...
Popular Science

Biologists discover gene that may determine ‘good’ and ‘bad’ dads

Breakthroughs, discoveries, and DIY tips sent six days a week. Terms of Service and Privacy Policy. Most mammals grow up in single parent homes. It’s estimated that ...
FierceBiotech

UPDATED: FDA illuminates new approval pathway for bespoke gene editing therapies

After teasing a new regulatory process for personalized genetic medicines at the end of last year, the FDA today unveiled draft guidance for an approval pathway that could see custom CRISPR therapies, ...
Reuters

US FDA proposes framework to speed rare disease gene therapy approvals

WASHINGTON, Feb 23 (Reuters) - The U.S. Food and Drug Administration proposed on Monday a new framework to speed approvals of personalized treatments for rare and life-threatening genetic diseases, ...
STAT

FDA unveils rules for bespoke gene therapies, predicting flood of rare disease applications

Jason Mast is a general assignment reporter at STAT focused on the science behind new medicines and the systems and people that decide whether that science ever reaches patients. You can reach Jason ...

Penn medical student with rare genetic form of ALS on mission to develop gene therapy

Yentli Soto Albrecht has a rare genetic form of ALS and is working on research at Penn that could one day prove life-saving.
NPR

The FDA creates a quicker path for gene therapies

The Food and Drug Administration Monday unveiled the details of a new policy designed to make it easier and quicker for patients with very rare diseases to get cutting-edge treatments. The new ...
C&EN

The Chemistry of Genome Editing: Transforming Human and Planet Health with CRISPR

I was born in Washington, DC, in 1964, the oldest of three sisters, but the place that truly formed me as a scientist was Hilo, on the Big Island of Hawaii. Growing up there, far from the mainland ...