A boy in Maryville is facing a challenge that most kids will never experience. It's a rare genetic disorder that causes ...
Duchenne therapy may be evolving from slowing disease to reversing it—with RNA approaches offering the prospect of restoring ...
STATEN ISLAND, N.Y. — Those who participated in “The 13th annual Michael 2025 Step For A Cure 5k Run And Walk” at the FDR ...
A gene therapy treatment brings hope to 9-year-old Will Leko, diagnosed with Duchenne Muscular Dystrophy, as his family continues to navigate ongoing challenges.
On Sunday, Oct. 5, from noon to 5 p.m., the Skyline Beer Company at 98 Southwick Road in Westfield will be hosting “Wheels ...
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Tevard Biosciences, Inc., a privately held biotechnology company pioneering tRNA-based therapies to cure a broad range of ...
Two months after its treatment for Duchenne-related cardiomyopathy was rejected, the company aligned with the agency on a ...
Data from ongoing DELIVER trial demonstrated sustained functional improvement through 18 months; results from Registrational Expansion Cohort ...
President Donald Trump demanded drugmakers voluntarily lower prices for some of their drugs to match what they charge other ...
The CureDuchenne Clinic, in partnership with Children’s Hospital of Orange County (now part of Rady Children’s Health), ...
Aurinia Pharmaceuticals (AUPH) stock gains as the company defends its lead drug Lupkynis after a top FDA regulator linked it ...
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