One of those things is the CureDuchenne clinic in Denton. It provides care to underserved and uninsured people with Duchenne. "I think it's good that we're trying to find the cure," Shep said.

MISSISSAUGA, ON, Oct. 2, 2025 /CNW/ – Kye Pharmaceuticals (“Kye”) announced today that Health Canada has approved AGAMREE ® (vamorolone) for the treatment of Duchenne Muscular Dystrophy (DMD) in boys ...

Approximately 16 boys with Duchenne Muscular Dystrophy (DMD), including several teenagers, are set to benefit from the drug, givinostat. Patients will have to meet certain criteria, including being ...

Capricor Therapeutics is advancing deramiocel (CAP-1002) for DMD cardiomyopathy. Click here to find out why CAPR stock is a Buy.

- Data from ongoing DELIVER trial demonstrated sustained functional improvement through 18 months; results from Registrational Expansion Cohort expected late 2025 - WALTHAM, Mass., Sept. 29, 2025 ...

After three patients died, the maker of an investigational gene therapy stopped shipments of the drug after it refused to pull the drug.

For Beau and JeanAnn Bryan, the fight to save their sons has become a race against time — and they’re calling on their community to help. The Tea family needs to raise $800,000 to move forward with a ...

FDA and Capricor aligned on endpoints for HOPE-3 pivotal trial HOPE-3 pivotal trial completed; topline data expected mid-Q4 2025 to support BLA resubmission Company preparing to resubmit CRL response ...

Duchenne therapy may be evolving from slowing disease to reversing it—with RNA approaches offering the prospect of restoring function.