Emily Blunt Calls AI Actress Tilly Norwood ‘Really Scary' and Warns Hollywood Agencies: ‘Don't Do That' The 'stupidity' of ...

A boy in Maryville is facing a challenge that most kids will never experience. It's a rare genetic disorder that causes ...

STATEN ISLAND, N.Y. — Those who participated in “The 13th annual Michael 2025 Step For A Cure 5k Run And Walk” at the FDR ...

Following completion of the conference, presentations will be available on the Scientific Publications & Presentations page of the Our Science section of the Company website, or by clicking here.

You may unsubscribe at any time. By signing up, you agree to our terms of use and privacy policy. This site is protected by ...

A gene therapy treatment brings hope to 9-year-old Will Leko, diagnosed with Duchenne Muscular Dystrophy, as his family continues to navigate ongoing challenges.

President Donald Trump demanded drugmakers voluntarily lower prices for some of their drugs to match what they charge other ...

On Sunday, Oct. 5, from noon to 5 p.m., the Skyline Beer Company at 98 Southwick Road in Westfield will be hosting “Wheels ...

Satellos Bioscience is planning a Phase 2 trial in the U.S. to test SAT-3247 in children with Duchenne who are able to walk.

Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, granted equity awards ...

The FDA has granted Fast Track designation to SAR446268 for the treatment of non-congenital myotonic dystrophy type 1.